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RNAi therapeutic

Showing 1 - 25 of >10,000

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PH1, Primary Hyperoxaluria, RNAi Therapeutic Trial in Worldwide (Lumasiran)

Active, not recruiting
  • PH1
  • +4 more
  • Bordeaux, France
  • +8 more
Jan 13, 2023

Transthyretin-mediated Amyloidosis With Cardiomyopathy, ATTR Amyloidosis With Cardiomyopathy Trial (Patisiran)

Available
  • Transthyretin-mediated Amyloidosis With Cardiomyopathy
  • ATTR Amyloidosis With Cardiomyopathy
  • (no location specified)
Aug 17, 2022

Nonalcoholic Steatohepatitis, NASH Trial in Worldwide (ALN-HSD, Placebo)

Active, not recruiting
  • Nonalcoholic Steatohepatitis
  • NASH
  • Huntington Park, California
  • +20 more
Aug 11, 2022

Hemophilia A, Hemophilia B Trial in Worldwide (Fitusiran (SAR439774))

Active, not recruiting
  • Hemophilia A
  • Hemophilia B
  • Fitusiran (SAR439774)
  • Ann Arbor, Michigan
  • +11 more
Aug 4, 2022

Amyloidosis Trial in Worldwide (Patisiran (ALN-TTR02))

Completed
  • Amyloidosis
  • Patisiran (ALN-TTR02)
  • La Mesa, California
  • +55 more
Jan 19, 2023

Acute Intermittent Porphyria Trial in Sweden, United Kingdom, United States (givosiran (ALN-AS1))

Completed
  • Acute Intermittent Porphyria
  • givosiran (ALN-AS1)
  • San Francisco, California
  • +4 more
Nov 9, 2021

Study of Transthyretin-Mediated Amyloidosis

Recruiting
  • Transthyretin-Mediated Amyloidosis
  • ATTR Amyloidosis
    • La Jolla, California
    • +23 more
    Jan 13, 2023

    Patisiran in Polyneuropathy of ATTRv Amyloidosis WithV122I or

    Active, not recruiting
    • Hereditary Transthyretin-mediated (ATTRv) Amyloidosis
    • Polyneuropathy
    • Los Angeles, California
    • +26 more
    Mar 4, 2022

    Primary Hyperoxaluria Type 3 Trial in Worldwide (DCR-PHXC, Sterile Normal Saline (0.9% NaCl))

    Completed
    • Primary Hyperoxaluria Type 3
    • Boston, Massachusetts
    • +5 more
    Sep 9, 2021

    Idiopathic Pulmonary Fibrosis Trial in Adelaide (SRN-001, Placebo)

    Not yet recruiting
    • Idiopathic Pulmonary Fibrosis
    • Adelaide, South Australia, Australia
      CMAX Clinical Research
    Aug 2, 2023

    STARD3 in Colorectal Cancer: The STAR Study

    Recruiting
    • Colorectal Cancer
      • Aviano, Pordenone, Italy
        Centro di Riferimento Oncologico (CRO) di Aviano - IRCCS
      Nov 16, 2023

      Normal Physiology Trial run by the NIAID (Methylprednisolone sodium succinate(Solu-Medrol), Topical methylprednisolone (Advantan

      Completed
      • Normal Physiology
      • Methylprednisolone sodium succinate(Solu-Medrol)
      • Topical methylprednisolone (Advantan emulsion 0 /1%)
      • Bethesda, Maryland
        National Institutes of Health Clinical Center
      Nov 18, 2022

      Cardiac Amyloidosis : Diagnostic Using Red Flag Signals

      Recruiting
      • Cardiac Amyloidosis
      • diagnostic algorithm
      • Basse-Terre, Guadeloupe
      • +2 more
      Nov 16, 2020

      Hepatitis B, Chronic Trial in Worldwide (JNJ-73763989, JNJ-64300535, ETV monohydrate)

      Active, not recruiting
      • Hepatitis B, Chronic
      • Edegem, Belgium
      • +12 more
      Jan 17, 2023

      Hepatitis B, Chronic Trial in Worldwide (JNJ-73763989, PegIFN-alpha-2a, Tenofovir disoproxil)

      Terminated
      • Hepatitis B, Chronic
      • Hillsborough, New Jersey
      • +11 more
      Dec 28, 2022

      Metabolic Syndrome, Protection Against Trial in Castellana Grotte (Table Grape supplement)

      Active, not recruiting
      • Metabolic Syndrome, Protection Against
      • Table Grape supplement
      • Castellana Grotte, Bari, Italy
        IRCCS Saverio de Bellis
      Mar 20, 2022

      Lumbar Spine Stenosis Specimens for Identification of

      Not yet recruiting
      • Lumbar Spinal Stenosis
      • +5 more
      • Tc99-PYP or Tc99-HDMP Scan
      • Beverly Hills, California
      • +5 more
      Sep 12, 2023

      Primary Hyperoxaluria Type 1 (PH1) Trial in Worldwide (Placebo, Lumasiran)

      Active, not recruiting
      • Primary Hyperoxaluria Type 1 (PH1)
      • San Diego, California
      • +15 more
      Mar 4, 2022

      Hemophilia A, Hemophilia B Trial in Worldwide (fitusiran, Bypassing agents)

      Completed
      • Hemophilia A
      • Hemophilia B
      • Phoenix, Arizona
      • +57 more
      Mar 15, 2022

      Hemophilia A, Hemophilia B Trial in Worldwide (fitusiran, factor concentrates)

      Completed
      • Hemophilia A
      • Hemophilia B
      • Little Rock, Arkansas
      • +63 more
      Mar 15, 2022

      Morpho-functional Cardiac Modifications in Treated Mutated

      Unknown status
      • Cardiac Amyloidosis
        • Firenze, Italy
        • +1 more
        May 12, 2020

        Smokers Trial in Valencia (Therapeutic exercise program plus action observation training, Therapeutic exercise program plus sham

        Recruiting
        • Smokers
        • Therapeutic exercise program plus action observation training
        • Therapeutic exercise program plus sham action observation training
        • Valencia, Spain
          Universitat de Valencia
        Nov 7, 2023

        Smokers Trial in Valencia (Theapeutic exercise plus action observation training, Therapeutic exercise plus sham observation

        Recruiting
        • Smokers
        • Theapeutic exercise plus action observation training
        • Therapeutic exercise plus sham observation training
        • Valencia, Spain
          Universitat de Valencia
        Oct 24, 2023

        Melanoma Trial in Napoli (Vemurafenib, Peg-interferon, Cobimetinib)

        Completed
        • Melanoma
        • Napoli, Italy
          Fondazione G.Pascale
        Feb 23, 2022

        Chronic Pain, Neck Pain Trial in Almería (Monopolar electrical diathermy plus therapeutic yoga, Therapeutic Yoga)

        Recruiting
        • Chronic Pain
        • Neck Pain
        • Monopolar electrical diathermy plus therapeutic yoga
        • Therapeutic Yoga
        • Almería, Almeria, Spain
          Adelaida María Castro Sánchez
        Oct 2, 2023