RNAi therapeutic
Showing 1 - 25 of >10,000
Transthyretin-mediated Amyloidosis With Cardiomyopathy, ATTR Amyloidosis With Cardiomyopathy Trial (Patisiran)
Available
- Transthyretin-mediated Amyloidosis With Cardiomyopathy
- ATTR Amyloidosis With Cardiomyopathy
- (no location specified)
Aug 17, 2022
Nonalcoholic Steatohepatitis, NASH Trial in Worldwide (ALN-HSD, Placebo)
Active, not recruiting
- Nonalcoholic Steatohepatitis
- NASH
- ALN-HSD
- Placebo
-
Huntington Park, California
- +20 more
Aug 11, 2022
Hemophilia A, Hemophilia B Trial in Worldwide (Fitusiran (SAR439774))
Active, not recruiting
- Hemophilia A
- Hemophilia B
- Fitusiran (SAR439774)
-
Ann Arbor, Michigan
- +11 more
Aug 4, 2022
Amyloidosis Trial in Worldwide (Patisiran (ALN-TTR02))
Completed
- Amyloidosis
- Patisiran (ALN-TTR02)
-
La Mesa, California
- +55 more
Jan 19, 2023
Acute Intermittent Porphyria Trial in Sweden, United Kingdom, United States (givosiran (ALN-AS1))
Completed
- Acute Intermittent Porphyria
- givosiran (ALN-AS1)
-
San Francisco, California
- +4 more
Nov 9, 2021
Study of Transthyretin-Mediated Amyloidosis
Recruiting
- Transthyretin-Mediated Amyloidosis
- ATTR Amyloidosis
-
La Jolla, California
- +23 more
Jan 13, 2023
Patisiran in Polyneuropathy of ATTRv Amyloidosis WithV122I or
Active, not recruiting
- Hereditary Transthyretin-mediated (ATTRv) Amyloidosis
- Polyneuropathy
-
Los Angeles, California
- +26 more
Mar 4, 2022
Primary Hyperoxaluria Type 3 Trial in Worldwide (DCR-PHXC, Sterile Normal Saline (0.9% NaCl))
Completed
- Primary Hyperoxaluria Type 3
- DCR-PHXC
- Sterile Normal Saline (0.9% NaCl)
-
Boston, Massachusetts
- +5 more
Sep 9, 2021
Idiopathic Pulmonary Fibrosis Trial in Adelaide (SRN-001, Placebo)
Not yet recruiting
- Idiopathic Pulmonary Fibrosis
- SRN-001
- Placebo
-
Adelaide, South Australia, AustraliaCMAX Clinical Research
Aug 2, 2023
STARD3 in Colorectal Cancer: The STAR Study
Recruiting
- Colorectal Cancer
-
Aviano, Pordenone, ItalyCentro di Riferimento Oncologico (CRO) di Aviano - IRCCS
Nov 16, 2023
Normal Physiology Trial run by the NIAID (Methylprednisolone sodium succinate(Solu-Medrol), Topical methylprednisolone (Advantan
Completed
- Normal Physiology
- Methylprednisolone sodium succinate(Solu-Medrol)
- Topical methylprednisolone (Advantan emulsion 0 /1%)
-
Bethesda, MarylandNational Institutes of Health Clinical Center
Nov 18, 2022
Cardiac Amyloidosis : Diagnostic Using Red Flag Signals
Recruiting
- Cardiac Amyloidosis
- diagnostic algorithm
-
Basse-Terre, Guadeloupe
- +2 more
Nov 16, 2020
Hepatitis B, Chronic Trial in Worldwide (JNJ-73763989, JNJ-64300535, ETV monohydrate)
Active, not recruiting
- Hepatitis B, Chronic
- JNJ-73763989
- +4 more
-
Edegem, Belgium
- +12 more
Jan 17, 2023
Metabolic Syndrome, Protection Against Trial in Castellana Grotte (Table Grape supplement)
Active, not recruiting
- Metabolic Syndrome, Protection Against
- Table Grape supplement
-
Castellana Grotte, Bari, ItalyIRCCS Saverio de Bellis
Mar 20, 2022
Lumbar Spine Stenosis Specimens for Identification of
Not yet recruiting
- Lumbar Spinal Stenosis
- +5 more
- Tc99-PYP or Tc99-HDMP Scan
-
Beverly Hills, California
- +5 more
Sep 12, 2023
Primary Hyperoxaluria Type 1 (PH1) Trial in Worldwide (Placebo, Lumasiran)
Active, not recruiting
- Primary Hyperoxaluria Type 1 (PH1)
- Placebo
- Lumasiran
-
San Diego, California
- +15 more
Mar 4, 2022
Hemophilia A, Hemophilia B Trial in Worldwide (fitusiran, Bypassing agents)
Completed
- Hemophilia A
- Hemophilia B
- fitusiran
- Bypassing agents
-
Phoenix, Arizona
- +57 more
Mar 15, 2022
Hemophilia A, Hemophilia B Trial in Worldwide (fitusiran, factor concentrates)
Completed
- Hemophilia A
- Hemophilia B
- fitusiran
- factor concentrates
-
Little Rock, Arkansas
- +63 more
Mar 15, 2022
Morpho-functional Cardiac Modifications in Treated Mutated
Unknown status
- Cardiac Amyloidosis
-
Firenze, Italy
- +1 more
May 12, 2020
Smokers Trial in Valencia (Therapeutic exercise program plus action observation training, Therapeutic exercise program plus sham
Recruiting
- Smokers
- Therapeutic exercise program plus action observation training
- Therapeutic exercise program plus sham action observation training
-
Valencia, SpainUniversitat de Valencia
Nov 7, 2023
Smokers Trial in Valencia (Theapeutic exercise plus action observation training, Therapeutic exercise plus sham observation
Recruiting
- Smokers
- Theapeutic exercise plus action observation training
- Therapeutic exercise plus sham observation training
-
Valencia, SpainUniversitat de Valencia
Oct 24, 2023
Chronic Pain, Neck Pain Trial in Almería (Monopolar electrical diathermy plus therapeutic yoga, Therapeutic Yoga)
Recruiting
- Chronic Pain
- Neck Pain
- Monopolar electrical diathermy plus therapeutic yoga
- Therapeutic Yoga
-
Almería, Almeria, SpainAdelaida María Castro Sánchez
Oct 2, 2023